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Molecular Mechanisms of Microbial Pathogenesis

Chapter 125 | Part 5: Infectious Diseases · Part 5 – Infectious Diseases: Bacterial · Chapter 125


Key Clinical Points

  1. Infectious diseases occur when a live pathogen enters or a toxic pathogen product is ingested by the host.
  2. The infection process involves a multi-step progression: microbial entry (colonization), attachment in favored niches, immune evasion, replication, and transmission.
  3. Bacterial attachment to host tissues relies on receptor–ligard interactions mediated by pili (Type I, IV), flagella, and autotransporter proteins.
  4. The Type III Secretion System (T3SS) functions as a 'needle-and-syringe' mechanism to deliver effector proteins into eukaryotic cells (e.g., Salmonella, Shigella).
  5. Bacteria utilize diverse strategies for nutrient acquisition in nutrient-poor infection sites.
  6. The complement system is a critical innate defense; pathogens often evolve mechanisms to target and evade specific points of the cascade, including opsonization and Membrane Attack Complex (MAC) formation.
  7. Biofilms provide protection against immune clearance and significantly hinder antibiotic penetration.
  8. Host factors such as CFTR mutations or FUT2 deficiency significantly influence susceptibility to specific infections.
  9. Pathogen tropism determines the clinical site of infection (e.g., S. aureus in soft tissue, M. tuberculosis in the respiratory tract).

1. DEFINITION & OVERVIEW

Core Concept: The study of infectious diseases focuses on host–microbial interactions, reflecting an evolutionary arms race between pathogens and the immune system. • Infection Process: - Microbial entry (colonization) - Attachment in favored niches - Immune evasion - Deployment of virulence factors causing tissue damage - Transmission to new hosts - Modulation by host microbiota


2. EPIDEMIOLOGY

Global Impact: Infectious diseases account for approximately 1/6 of global deaths. • Emerging Threats: Includes SARS-CoV-2, mpox, and viral hemorrhagic fevers. • Biosecurity: Microbial bioterrorism remains a significant threat. • Host Genetics: Cystic fibrosis (CF) prevalence (>2.5% in Caucasians) is linked to increased resistance against Salmonella Typhi due to CFTR receptor interactions.


3. ETIOLOGY & PATHOPHYSIOLOGY

Entry Routes: Skin/mucosal barriers, respiratory droplets, gastrointestinal ingestion, genitourinary colonization. • Pathogen Types: - Preformed toxins (e.g., S. aureus enterotoxins, botulinum toxin) - Live pathogens with tissue-specific tropism (e.g., Group A streptococci cause pharyngitis but not pneumonia). • Table 125-1: Lists bacterial pathogens, associated diseases, and tissue tropism.

Table 125-1 Bacterial Pathogens, Diseases, and Niches

MOST COMMON TROPISM BACTERIUM DISEASE
Skin, respiratory tract, small intestine Bacillus anthracis Anthrax
Respiratory tract Bordetella pertussis
Systemic Borrelia burgdorferi Lyme disease
Systemic Brucella abortus
Systemic Burkholderia pseudomallei Melioidosis
Eyes, venereal Chlamydia trachomatis Various chlamydioses
Colon Clostridioides difficile Colitis
Colon Corynebacterium diphtheriae Diphtheria
Systemic Coxiella burnetii Q fever
Colon Enterohemorrhagic Escherichia coli
Stomach Helicobacter pylori Gastritis, gastric ulcers
Respiratory tract Legionella pneumophila Legionnaires’ disease
Systemic, central nervous system Listeria monocytogenes Listeriosis
Respiratory tract Mycobacterium tuberculosis Tuberculosis
Urogenital tract Neisseria gonorrhoeae Gonorrhea
Respiratory tract Pseudomonas aeruginosa Pneumonia
Systemic Salmonella enterica serovar Typhi Typhoid fever
Systemic Salmonella enterica serovar Typhimurium Typhoid fever
Colon, rectum Shigella spp. Dysentery, shigellosis
Soft tissue Staphylococcus aureus Skin infection
Soft tissue Group A Streptococcus Soft tissue infection
Small intestine Vibrio cholerae Cholera
Systemic Yersinia pestis Plague

Table 125-2 Classes of Bacterial Adhesion Proteins and Their Host Receptors

ADHESIN EXAMPLE RECEPTOR
Type I pili Fim protein, uropathogenic Escherichia coli Terminal mannose of uroplakin N-glycan in urinary epithelial cells
Type P pili Pap protein, uropathogenic E. coli
Type IV pili Tfp protein, Neisseria gonorrhoeae CD64, CR3, I domain–containing integrins
Opa Opa protein, Neisseria meningitidis CEACAMsa
MSCRAMM SdrC protein, Staphylococcus aureus β-Neurexin
Flagellum FliC protein, Pseudomonas aeruginosa Asialo-GM1 ganglioside
Autotransporter Invasin, Yersinia pseudotuberculosis β1-Integrins
Autotransporter Ag85, Mycobacterium tuberculosis Fibronectin

3.1 Attachment Mechanisms

Receptor–Ligand Interaction: Critical for niche establishment. • Adhesin Types: - Pili: Type I (e.g., E. coli to uroplakin N-glycan) and Type IV (e.g., N. gonorrhoeae to CD64, CR3, or integrins). - Flagella: Facilitate chemotaxis and adhesion (e.g., P. aeruginosa to Asialo-GM1). - Autotransporters: Mediate intimate interactions (e.g., Invasin in Y. pseudotuberculosis to β1-Integrins; Ag85 in M. tuberculosis to Fibronectin). • Table 125-2: Details specific adhesin classes and their corresponding host receptors (e.g., Opa protein binding to CEACAMsa).

3.2 Mechanisms of Microbial Entry

Trigger Mechanism: - Pathogens: Shigella, Salmonella spp. - Pathway: T3SS → delivery of effector proteins → cytoskeleton manipulation → formation of membrane ruffles → endocytosis. • Zipper Mechanism: - Pathogens: Yersinia, Listeria spp. - Pathway: Bacterial surface proteins → host receptor clustering → 'zipping' of the membrane → uptake in a tightly opposed vacuole. • Intracellular Movement: Actin-based motility enables cell-to-cell spread (e.g., L. monocytogenes, Rickettsia).

3.3 Survival in the Vacuole

Endosomal Subversion: Bacterial effector proteins prevent maturation (e.g., L. pneumophila phospholipase VipD). - T4SS systems deliver proteins to alter vacuolar environments. • Escape Strategies: - L. monocytogenes: Uses listeriolysin O. - Shigella: Utilizes T3SS for escape. • Innate Immune Recognition: - Autophagy (Xenophagy): Detection of invasion or nutrient depletion → phagophore formation → autophagosome → fusion with lysosome → degradation. - Inflammasome Activation: Sensing of PAMPs/DAMPs → Inflammasome assembly → Caspase-1 activation → [Pro-inflammatory gene expression (IL-1β, IL-18)] and [Gasdermin D pore formation → K⁺ efflux → pyroptotic cell death]. • Table 125-3: Lists Pattern Recognition Receptors (PRRs) and their ligands (e.g., TLR2/Lipoproteins, TLR5/Flagellin, STING/Cyclic dinucleotides).


4. CLINICAL FEATURES

Tissue Tropism: Manifestations are determined by the specific site of infection (e.g., systemic vs. localized). • Toxin-Mediated Disease: Examples include botulism and cholera. • Chronic Carriage: Driven by successful immune evasion strategies.


5. DIFFERENTIAL DIAGNOSIS

Etiology Distinction: Differentiate bacterial vs. viral infections based on clinical presentation. • Mechanism Differentiation: Distinguish between toxin-mediated vs. invasive disease mechanisms. • Host Factor Influence: Consider host factors (e.g., CFTR mutations, FUT2 deficiency) that affect susceptibility.


6. INVESTIGATIONS & DIAGNOSIS

  1. Clinical Assessment: Evaluate symptoms based on tissue-specific manifestations.
  2. Microbiological Culture: Primary method for identifying pathogens and serotyping.
  3. Molecular Testing: Used for rapid identification and detection of specific virulence factors.
  4. Imaging: Utilized for abscess localization or assessing systemic involvement.
  5. Complement Assays: Used in research/clinical settings to study immune evasion.

7. MANAGEMENT & TREATMENT

  1. Antibiotic Therapy: Target specific virulence mechanisms (e.g., inhibiting T3SS or biofilm formation).
  2. Adjunctive Therapies: Use immunoglobulins for conditions like C. difficile.
  3. Biofilm Disruption: Strategies to overcome antibiotic resistance in chronic infections.
  4. Vaccination: Targeted at pathogens utilizing specific adhesins.

8. PROGNOSIS & COMPLICATIONS

Prognostic Factors: Determined by pathogen virulence, host immunity, and timing of treatment. • Common Complications: Sepsis, abscess formation, and chronic carriage. • Long-term Sequelae: e.g., postbotulism neuropathy in toxin-mediated cases.


9. SPECIAL CONSIDERATIONS

Cystic Fibrosis: Altered CFTR function → increased S. Typhi adherence. • Glycan Deficiency: FUT2 nonfunctional alleles → altered susceptibility to infection. • Microbiome Influence: Host microbiota modulates all stages of infection.


10. KEY PEARLS & CLINICAL TRAPS

T3SS Importance: Essential for bacterial intracellular survival and host cell manipulation. - Trigger mechanism (Salmonella/Shigella) vs. Zipper mechanism (Listeria/Yersinia). • Biofilms: Primary cause of antibiotic resistance in chronic infections. • Complement Evasion: A critical virulence mechanism; pathogens may inhibit specific points in the cascade to avoid opsonization or MAC formation.


TABLES

Table 125-3: Pattern Recognition Receptors of the Innate Immune System and Their Ligands | PATTERN RECOGNITION RECEPTOR | LIGAND OR MODE OF ACTIVATION | | --- | -- | | TLR2 (with TLR1 or TLR6) | Lipoproteins | | TLR5 | Flagellin | | NLRP1 | Enzymatic cleavage | | NLRP6 | Lipoteichoic acid, RNA | | STING | Cyclic dinucleotides | | NOD1 and NOD2 | |


Reference Tables

TABLE 124-5 Initial Empirical Antibiotic Therapy for Common Infectious Disease Presentations a

Harrison's 22e, p.964

CLINICAL SYNDROME COMMON ETIOLOGIES ANTIBIOTIC(S) COMMENTS SEE CHAPTER(S)
Skin and soft tissue
infection
S. aureus, Streptococcus
pyogenes
Dicloxacillin, 250–500 mg PO qid
or
Cephalexin, 250–500 mg PO qid
or
Clindamycin, 300–450 mg PO tid
or
Nafcillin/oxacillin, 1–2 g q4h
If MRSA is a consideration,
clindamycin, vancomycin (15
mg/kg q12hb), linezolid (600 mg
IV/PO q12h), or TMP-SMX
(1–2 double-strength tablets PO
bidg) can be used.
134 and pathogen-
specific chapters
125 Molecular Mechanisms of
Microbial Pathogenesis
Jordan B. Jastrab, Marcia B. Goldberg

TABLE 125-1 Bacterial Pathogens, Diseases, and Niches

Harrison's 22e, p.965

MOST COMMON
TROPISM
BACTERIUM DISEASE
Skin, respiratory tract,
small intestine
Bacillus anthracis Anthrax
Bordetella pertussis
Systemic Borrelia burgdorferi Lyme disease
Brucella abortus
Systemic Burkholderia pseudomallei Melioidosis
Chlamydia trachomatis
Colon Clostridioides difficile Colitis
Corynebacterium
diphtheriae
Systemic Coxiella burnetii Q fever
Enterohemorrhagic
Escherichia coli
Stomach Helicobacter pylori Gastritis, gastric ulcers
Legionella pneumophila
Systemic, central
nervous system
Listeria monocytogenes Listeriosis
Mycobacterium tuberculosis
Urogenital tract Neisseria gonorrhoeae Gonorrhea
Pseudomonas aeruginosa
Systemic Salmonella enterica serovar
Typhi
Typhoid fever
Salmonella enterica serovar
Typhimurium
Colon, rectum Shigella spp. Dysentery, shigellosis
Staphylococcus aureus
Soft tissue Group A Streptococcus
Vibrio cholerae
Systemic Yersinia pestis Plague

TABLE 125-2 Classes of Bacterial Adhesion Proteins and Their Host Receptors ADHESIN Type I pili

Harrison's 22e, p.966

ADHESIN EXAMPLE RECEPTOR
Type I pili Fim protein, uropathogenic
Escherichia coli
Terminal mannose of
uroplakin N-glycan in
urinary epithelial cells
Pap protein, uropathogenic E. coli
Type IV pili Tfp protein, Neisseria
gonorrhoeae
CD64, CR3, I domain–
containing integrins
SdrC protein, Staphylococcus
aureus
Opa Opa protein, Neisseria
meningitidis
CEACAMsa
FliC protein, Pseudomonas
aeruginosa
Autotransporter Invasin, Yersinia
pseudotuberculosis
β1-Integrins
Ag85, Mycobacterium
tuberculosis

TABLE 125-3 Pattern Recognition Receptors of the Innate Immune System and Their Ligands

Harrison's 22e, p.971

PATTERN RECOGNITION RECEPTOR LIGAND OR MODE OF ACTIVATION
TLR2 (with TLR1 or TLR6) Lipoproteins
TLR5 Flagellin
NLRP1 Enzymatic cleavage
NLRP6 Lipoteichoic acid, RNA
STING Cyclic dinucleotides